Press Release

Phenylketonuria Treatment Market to grow with a CAGR of 8.25% through 2030

Increasing healthcare infrastructure and a supportive regulatory environment are the major drivers for the Global Phenylketonuria Treatment Market in the forecast period, 2026-2030F

 

According to TechSci Research report, “Phenylketonuria Treatment Market - Global Industry Size, Share, Trends, Competition, Opportunity and Forecast, 2030F”, Global Phenylketonuria Treatment Market was valued at USD 502.18 million in 2024 and is anticipated to witness an impressive growth in the forecast period with a CAGR of 8.25% through 2030F.  This can be due to collaborations and partnerships among leading companies with a diverse approach to merge the expertise of individual companies and to strengthen their position in the market.

Advancements in the treatment of Phenylketonuria (PKU) have been ongoing, with a focus on improving the management of this genetic disorder. PKU is characterized by the inability to metabolize phenylalanine, an amino acid found in protein-containing foods. The treatment aims to maintain safe blood phenylalanine levels while ensuring adequate nutrition. Glycomacropeptide (GMP) based protein substitutes have been developed as an alternative to traditional amino acid-based medical foods.

GMP is a naturally low-phenylalanine protein derived from cheese whey. Advances in the formulation of protein substitutes have led to better-tasting and more convenient products, improving patient compliance. Companies have introduced low-protein food products specifically designed for PKU patients, making it easier to adhere to dietary restrictions. PEGylated Phenylalanine Ammonia Lyase (PAL) has been developed to help break down excess phenylalanine in the blood. These therapies are administered by injection and can be effective in managing PKU.

An uncommon hereditary condition called phenylketonuria (PKU) causes elevated blood levels of the amino acid phenylalanine. Proteins derived from food and nutrition include the amino acid phenylalanine. In the human body, the phenylalanine hydroxylase enzyme transforms phenylalanine into the amino acid tyrosine. Seizures, mental illnesses, and several other untreated disorders can be brought on by an excess of phenylalanine in the blood.

 

Browse over XX market data Figures and spread through XX Pages and an in-depth TOC on "Phenylketonuria Treatment Market

 

Global Phenylketonuria Treatment Market segmentation is based on route of administration, product, distribution channel, region and company.

Based on Distribution Channel, The Global Phenylketonuria (PKU) Treatment Market is witnessing rapid growth, with the Online Pharmacies segment emerging as the fastest-growing during the forecast period. The increasing preference for convenience, privacy, and accessibility is driving patients and caregivers toward digital platforms for purchasing PKU medications and specialized low-protein medical foods. Online pharmacies offer a wider range of treatment options, allow for easy price comparisons, and enable discreet transactions—all of which are highly valued in managing rare conditions like PKU. As digital health adoption accelerates, this segment is experiencing significant momentum and expanding at a robust pace.

Based on Region, Asia-pacific region to fastest growth in the Global Phenylketonuria Treatment Market. Awareness of rare genetic disorders like PKU has been growing in the Asia-Pacific region. As awareness increases, more individuals may be diagnosed with PKU through newborn screening programs and genetic testing, driving demand for treatment. The Asia-Pacific region is home to a significant portion of the world's population. As the population grows, so does the number of individuals potentially affected by PKU, contributing to increased demand for PKU treatments. Many countries in the Asia-Pacific region are experiencing rapid economic growth, leading to increased healthcare infrastructure and resources. This growth can improve access to specialized care and PKU treatments


Some of the major companies operating in the Global Phenylketonuria Treatment Market include:

  • BioMarin Pharmaceutical Inc.
  • Synlogic, Inc.
  • Retrophin, Inc.
  • Daiichi Sankyo Company, Limited
  • Codexis, Inc.
  • SOM Innovation Biotech SL
  • Homology Medicines, Inc.


Download Free Sample Report

Customers can also request 10% free customization on this report

 

“North America is expected to drive significant demand for phenylketonuria (PKU) treatment, fueled by increasing awareness, advanced healthcare infrastructure, and supportive government initiatives. The presence of well-established pharmaceutical companies committed to enhancing patient well-being further accelerates market growth. Ongoing research and development efforts, including innovative drug formulations and improved dietary management solutions, contribute to expanding treatment options. Rising newborn screening programs and early diagnosis rates boost the demand for effective PKU therapies. These factors, combined with a highly competitive market landscape, are expected to drive substantial growth in the global PKU treatment market during the forecast period" said Mr. Karan Chechi, Research Director of TechSci Research, a research-based Global management consulting firm.

"Phenylketonuria Treatment Market - Global Industry Size, Share, Trends, Opportunity, and Forecast, Segmented By Route of Administration (Oral, Parenteral), By Product (Dietary Supplement, Drugs), By Distribution Channel (Hospital Pharmacies, Online Pharmacies, Pediatric Clinics), By Region & Competition 2020-2030F", evaluated the future growth potential of Global Phenylketonuria Treatment Market and provides statistics & information on market size, structure, and future market growth. The report intends to provide innovative market intelligence and help decision makers take sound investment decisions. Besides, the report also identifies and analyzes the emerging trends along with essential drivers, challenges, and opportunities in Global Phenylketonuria Treatment Market.

 

Contact

TechSci Research LLC

420 Lexington Avenue, Suite 300,

New York, United States- 10170

Tel: +1-332-258-6602

Email: [email protected]

Website: www.techsciresearch.com

Relevant News